1 projets européens trouvés
Recherche sur 125080 projets européens
TERMINÉ
Developing new therapies for Batten disease (BATCure)
Date du début: 1 janv. 2016, Date de fin: 31 déc. 2018,
The goal of BATCure is to advance the development of new therapeutic options for a group of rare lysosomal diseases - neuronal ceroid lipofuscinoses (NCL) or Batten disease. There are > thousand affected across Europe, with a combined incidence of c.1:100 000. The NCLs are devastating and debilitating genetic disorders that mainly affect children, who suffer progressive dementia and motor decline, ...
Voir le projet