2 projets européens trouvés
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TERMINÉ
Clinical trial of gene therapy for MPS VI - a severe lysosomal storage disorder (MEUSIX)
Date du début: 1 déc. 2012, Date de fin: 30 nov. 2017,
"Mucopolysaccharidosis VI (MPS VI, or Maroteaux-Lamy syndrome; OMIM #253200) is a rare lysosomal storage disease caused by deficient activity of arylsulfatase B (ARSB). MPS VI is characterized by growth retardation, corneal clouding, cardiac valve disease, organomegaly, skeletal dysplasia, without central nervous system involvement. Thus, systemic therapies targeting peripheral organs have the pot ...
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Participants partenaires
TERMINÉ
Collaborative HIV and Anti-HIV Drug Resistance Network (CHAIN)
Date du début: 1 avr. 2009, Date de fin: 31 mars 2014,
...s and supporting evidence-based public health policy and action. CHAIN brings together Europe’s leading internationally recognised scientific expertise in basic science, molecular epidemiology, bioinformatics and surveillance of HIV and HIV resistance including the WHO, strong links to Eastern Europe through the existing FP6 funded cohort network Europe HIVresistance and strategic links to releva ...
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